Parents of children with rare, incurable diseases have long had to deal with dual sources of hopelessness: the helpless feeling that their child was sick, and the compounding dread of knowing that few treatments were likely forthcoming.
But for one such group of parents, new hope exists thanks to a remarkable breakthrough pioneered by Krystof Bankiewicz, MD, PhD, vice chair of research at The Ohio State University College of Medicine.
Dr. Bankiewicz, who has deep roots in the field of gene therapy, helped develop a therapy that is bringing the ability to walk and talk to children around the world who were born with neither.
In the words of one very grateful mother whose son benefited from this breakthrough: “He’s completely changing the lives of these children, and it is absolutely astounding.”
Read more on Dr. Bankiewicz and how his work can affect countless other neurological patients at Health & Discovery.
